Outcomes of Gene Therapy for Severe Sickle Disease and Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral Beta AT87Q-Globin Vector.

Blood

Marina Cavazzana, Jean-Antoine Ribeil, Emmanuel Payen, Felipe Suarez, Yves Beuzard, Fabien Touzot, Resy Cavallesco, Francois Lefrere, Stany Chretien, Philippe Bourget, Fabrice Monpoux, Corinne Pondarre, Benedicte Neven, Manfred Schmidt, Christof von Kalle, Frans A. Kuypers, Laura Sandler, Sandeep Soni, Olivier Hermine, Stephane Blanche, Mariane De Montalembert, Salima Hacien-Bey-Abina, Philippe Leboulch. Outcomes of Gene Therapy for Severe Sickle Disease and Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral Beta AT87Q-Globin Vector. Blood. 2015 Dec 3; 126(23):202-202.

2015
https://researcherprofiles.org/profile/425025967

Marina Cavazzana, Jean-Antoine Ribeil, Emmanuel Payen, Felipe Suarez, Yves Beuzard, Fabien Touzot, Resy Cavallesco, Francois Lefrere, Stany Chretien, Philippe Bourget, Fabrice Monpoux, Corinne Pondarre, Benedicte Neven, Manfred Schmidt, Christof von Kalle, Frans A. Kuypers, Laura Sandler, Sandeep Soni, Olivier Hermine, Stephane Blanche, Mariane De Montalembert, Salima Hacien-Bey-Abina, Philippe Leboulch